European consensus for starting and stopping enzyme replacement therapy in adult patients with Pompe disease: a 10-year experience
- Authors: van der Ploeg A.T.1, Kruijshaar M.У.1, Toscano A.2, Laforet P.3, Angelini C.4, Lachmann R.H.5, Pascual Pascual S.I.6,7, Roberts M.8, Rosler K.9, Stulnig T.10, van Doorn P.A.11, Van den Bergh P.12, Vissing J.13, Schoser B.14
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Affiliations:
- Center for Lysosomal and Metabolic Diseases, Erasmus MC University Medical Center
- Department of Clinical and Experimental Medicine, University of Messina
- Paris-Est, Referral Center for Neuromuscular Disorders, Pitie-Salpetriere Hospital, Assistance Publique Hopitaux de Paris
- Angelini Fondazione S. Camillo Hospital, IRCCS
- Charles Dent Metabolic Unit, National Hospital for Neurology and Neurosurgery
- Servicio de Neuropediatria, Hospital Universitario La Paz
- Department of Paediatrics, Universidad Autonoma de Madrid
- Department of Neurology, Salford Royal NHS Foundation Trust
- Salford
- Department of Medicine III, Medical University of Vienna
- Department of Neurology, Erasmus MC University Medical Center
- Department of Neurology, Neuromuscular Reference Centre, University Hospitals St-Luc
- Copenhagen Neuromuscular Center, Rigshospitalet, University of Copenhagen
- Friedrich-Baur-Institute, Ludwig-Maximilians-University
- Issue: Vol 8, No 4 (2018)
- Pages: 19-34
- Section: LECTURES AND REVIEWS
- Published: 11.01.2019
- URL: https://nmb.abvpress.ru/jour/article/view/301
- DOI: https://doi.org/10.17650/2222-8721-2018-8-4-19-34
- ID: 301
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Abstract
About the authors
A. T. van der Ploeg
Center for Lysosomal and Metabolic Diseases, Erasmus MC University Medical Center
Author for correspondence.
Email: a.vanderploeg@erasmusmc.nl
Rotterdam Netherlands
M. Ую Kruijshaar
Center for Lysosomal and Metabolic Diseases, Erasmus MC University Medical Center
Email: fake@neicon.ru
Rotterdam Netherlands
A. Toscano
Department of Clinical and Experimental Medicine, University of Messina
Email: fake@neicon.ru
Messina Italy
P. Laforet
Paris-Est, Referral Center for Neuromuscular Disorders, Pitie-Salpetriere Hospital, Assistance Publique Hopitaux de Paris
Email: fake@neicon.ru
Paris France
C. Angelini
Angelini Fondazione S. Camillo Hospital, IRCCS
Email: fake@neicon.ru
Venice Italy
R. H. Lachmann
Charles Dent Metabolic Unit, National Hospital for Neurology and Neurosurgery
Email: fake@neicon.ru
London United Kingdom
S. I. Pascual Pascual
Servicio de Neuropediatria, Hospital Universitario La Paz;Department of Paediatrics, Universidad Autonoma de Madrid
Email: fake@neicon.ru
Madrid Spain
M. Roberts
Department of Neurology, Salford Royal NHS Foundation Trust
Email: fake@neicon.ru
Salford United Kingdom
K. Rosler
Salford
Email: fake@neicon.ru
Bern Switzerland
T. Stulnig
Department of Medicine III, Medical University of Vienna
Email: fake@neicon.ru
Vienna Austria
P. A. van Doorn
Department of Neurology, Erasmus MC University Medical Center
Email: fake@neicon.ru
Rotterdam Netherlands
P.Y. K. Van den Bergh
Department of Neurology, Neuromuscular Reference Centre, University Hospitals St-Luc
Email: fake@neicon.ru
Brussels Belgium
J. Vissing
Copenhagen Neuromuscular Center, Rigshospitalet, University of Copenhagen
Email: fake@neicon.ru
Copenhagen Denmark
B. Schoser
Friedrich-Baur-Institute, Ludwig-Maximilians-University
Email: fake@neicon.ru
Munich Germany
References
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