For citations:
Popov K.D., Alekseeva T.M., Nazarov V.D., Vlasenko A.I., Malyshev S.M. Molecular markers of disease severity and response to nusinersen therapy in 5q spinal muscular atrophy (literature review). Neuromuscular Diseases. 2023;13(3):33-39. (In Russ.) https://doi.org/10.17650/2222-8721-2023-13-3-33-39