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Neuromuscular Diseases

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Artemyeva S.B., Papina Yu.O., Shidlovskaya O.A., Monakhova A.V., Vlodavets D.V. Experience of using gene replacement therapy with Zolgensma® (onasemnogene abeparvovec) in real clinical practice in Russia. Neuromuscular Diseases. 2022;12(1):29-38. https://doi.org/10.17650/2222-8721-2022-12-1-29-38



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ISSN 2222-8721 (Print)
ISSN 2413-0443 (Online)