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Neuromuscular Diseases

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Shchugareva L.M., Koroleva V.D., Poteshkina O.V. Experience of using onasemnogen abeparvovek in children with spinal muscular atrophy 5q with 2 or 3 copies of the SMN2 gene in a multidisciplinary center in Saint Petersburg. Neuromuscular Diseases. 2025;15(2):10-19. (In Russ.) https://doi.org/10.17650/2222-8721-2025-15-2-10-19

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ISSN 2222-8721 (Print)
ISSN 2413-0443 (Online)